Sandhoff disease research

Sandhoff disease research

Give online
to Sandhoff disease research

  • Sandhoff disease gene therapy
    Sandhoff disease gene therapy

Sandhoff dieease is a variation of the rare and usually fatal genetic disorder Tay-Sachs disease, which causes progressive damage to the nervous system.

Timothy Cox's research group is working to develop gene therapy for children who have inherited Sandhoff disease. In the most common form of Tay-Sachs condition, symptoms usually begin at around six months of age, when a previously normal child's development begins to slow and they gradually lose their ability to move. Mainly it is in Sandhoff disease models that gene therapy and other enhancing treatments have been first tried; they respond well to gene therapy, which is also being extended to Tay-Sachs disease as well.

Find out more

Sandhoff disease research website

Gift announcements

Cambridge owes its world-leading excellence in research and teaching to the generosity of its supporters. Our history is synonymous with a history of far-sighted benefaction, and the same is as true today as it has ever been.

Gift announcement
LycaHealth, the new healthcare brand, have presented a donation of £150,000 to Cambridge University to support Sri Lankan students and improve public health in Sri Lanka.   
Gift announcement
Multi-million pound legacy to create a new 'Ray and Dagmar Dolby Court' at Pembroke College

Impact of giving

Philanthropic giving is at the heart of the success of the Collegiate University, enabling us to make discoveries that change the world and to ensure that our students received an unrivalled education.

Wolfson Laser Lab
Philanthropic impact story
In 2016 the Department of Chemical Engineering and Biotechnology will bid farewell to central Cambridge and move into its new £60m purpose-built home on the West Cambridge Science and Technology Campus.
The new Laboratory of Molecular Biology at Addenbrooke's hospital
Philanthropic impact story
At any one time, more than 1000 clinical trials are being conducted across the Cambridge Biomedical Campus, the largest gathering of clinical, pharmaceutical and biomedical research specialists in Europe. These trials are a crucial step in the design of new medicines and medical devices – translating ideas that started in a research laboratory into new treatments for patients.